Financial assistance is gratefully acknowledged from:
Bayer
Biomarin Pharmaceutical
CSL Behring GmbH
F Hoffmann-La Roche
Grifols
Novo Nordisk Health Care AG
Octapharma AG
Pfizer Limited
Sanofi Genzyme
Sigilon Therapeutics
Sobi
Spark Therapeutics
Takeda
uniQure Inc.