Sponsors

Financial assistance is gratefully acknowledged from:

Bayer

Biomarin Pharmaceutical

CSL Behring GmbH

F Hoffmann-La Roche

Grifols

Novo Nordisk Health Care AG

Octapharma AG

Pfizer Limited

Sanofi Genzyme

Sigilon Therapeutics

Sobi

Spark Therapeutics

Takeda

uniQure Inc.